Positive news on Cystic Fibrosis on this year’s World Rare Disease Day.

World Rare Disease Day, on 28 February, is a reminder that 30 million Europeans and 300 million people worldwide live with rare diseases, including over 80,0000 patients with Cystic Fibrosis.

On World Rare Disease Day, the CHMP committee of the European Medicines Agency (EMA) announced a positive opinion on the extension of Kaftrio/Kadyceo in Europe to patients over 2 years of age with rare mutations. An important decision that paves the way for access to the breakthrough therapy in all European countries, as is already the case for Greek Cystic Fibrosis patients in our country.

Read the EMA statement here. Read the efforts of CF Europe and ECFS here.

Together with EURORDIS-Rare Diseases Europe and CF Europe we continue to stand by our patients! United we promote change and a fairer future and a life with Breathless Breath!

See more about World Rare Disease Day here.